{"id":6056,"date":"2025-01-30T14:32:51","date_gmt":"2025-01-30T13:32:51","guid":{"rendered":"https:\/\/www.ehc.eu\/non-classifiee\/ehc-publie-la-premiere-edition-de-novel-treatment-review-en-2025\/"},"modified":"2026-04-02T16:31:17","modified_gmt":"2026-04-02T14:31:17","slug":"ehc-publie-la-premiere-edition-de-novel-treatment-review-en-2025","status":"publish","type":"post","link":"https:\/\/www.ehc.eu\/fr\/nouvelles\/ehc-publie-la-premiere-edition-de-novel-treatment-review-en-2025\/","title":{"rendered":"EHC publie la premi\u00e8re \u00e9dition de Novel Treatment Review en 2025"},"content":{"rendered":"<!-- hero -->\t<section   class=\"subpage-hero bg-white\">\n\t\t<div class=\"container\">\n\t\t\t<div class=\"relative z-10\">\n\t\t\t\t<div class=\"pt-16 lg:pt-24 pb-24 lg:pb-32\">\n\t\t\t\t\t<div class=\"row justify-between gap-10 lg:gap-0 mt-10 text-center lg:text-left\">\n\t\t\t\t\t\t<div class=\"w-full lg:w-6\/12 lg:self-center\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"title h2\" data-scroll data-fade-up>\n\t\t\t\t\t\t\t\t\t<p class=\"text-[115%]\">EHC publie la premi\u00e8re \u00e9dition de Novel Treatment Review en 2025<\/p>\n\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t<\/div>\n\t\t\t\t\t\t\t\t\t<figure class=\"absolute size-[41.8rem] lg:size-[82.8rem] bottom-[-10%] right-[-10rem] lg:right-[-5%] image-contain opacity-100 skip-lazy\" data-parallax>\n\t\t\t\t\t<img decoding=\"async\" loading=\"eager\" src=\"https:\/\/etngbd86n6b.exactdn.com\/wp-content\/themes\/cbd\/img\/content-logo-colorfull-2.svg\" alt=\"content-logo-colorfull\">\n\t\t\t\t<\/figure>\n\t\t\t\t\t\t<\/section>\n<!-- overview -->\t<section   class=\"s-overlay-img s-padding bg-red\">\n\t\t<div class=\"container\">\n\t\t\t<div class=\"row w-full lg:flex-row justify-between text-center lg:text-left gap-14 lg:gap-0 relative z-10\">\n\t\t\t\t\t\t\t\t<div class=\"w-full lg:py-10\">\n\t\t\t\t\t<div class=\"bg-white min-h-full py-12 px-10 lg:py-24 lg:pl-24 xl:pl-44 relative radius-20 z-10\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"content mt-8\" data-scroll data-fade-up>\n\t\t\t\t\t\t\t\t<p>L\u2019EHC a publi\u00e9 le premier num\u00e9ro 2025 de <a href=\"https:\/\/academy.ehc.eu\/novel-treatment-product-reviews\/\" target=\"_blank\" rel=\"noopener\"><strong>sa Novel Treatment Review (NTR),<\/strong><\/a> une revue p\u00e9riodique des nouveaux traitements pour l\u2019h\u00e9mophilie, la maladie de von Willebrand et d\u2019autres troubles h\u00e9morragiques rares.<\/p>\n<p>L\u2019objectif du NTR est de fournir des informations \u00e0 jour \u00e0 notre communaut\u00e9 \u00e9largie, en particulier aux organisations nationales membres (NMO) de l\u2019EHC, ainsi qu\u2019un aper\u00e7u g\u00e9n\u00e9ral du paysage en rapide \u00e9volution du d\u00e9veloppement de produits de coagulation dans les troubles h\u00e9morragiques rares.<\/p>\n<p>Les principaux moments forts de cette derni\u00e8re \u00e9dition incluent :<\/p>\n<ul>\n<li>Concizumab (nom commercial Alhemo), un inhibiteur de la voie anti-facteur tissulaire (TFPI), a re\u00e7u une autorisation de mise en march\u00e9 de l\u2019UE.<\/li>\n<li>La Commission europ\u00e9enne a accord\u00e9 une autorisation de mise en march\u00e9 du marstacimab (nom commercial Hympavzi), destin\u00e9 \u00e0 la pr\u00e9vention des \u00e9pisodes de saignement chez les patients \u00e2g\u00e9s de 12 ans et plus, pesant au moins 35 kg, pr\u00e9sentant une h\u00e9mophilie s\u00e9v\u00e8re A ou B.<\/li>\n<li>Sangamo Therapeutics r\u00e9cup\u00e8re les droits de d\u00e9veloppement et de commercialisation du giroctocog\u00e8ne fitelparvovec, un produit de th\u00e9rapie g\u00e9nique exp\u00e9rimentale destin\u00e9 au traitement des adultes atteints d\u2019h\u00e9mophilie A mod\u00e9r\u00e9ment s\u00e9v\u00e8re \u00e0 s\u00e9v\u00e8re, suite \u00e0 la d\u00e9cision de Pfizer de mettre fin \u00e0 l\u2019accord mondial de collaboration et de licence entre les parties.<\/li>\n<li>Spark Therapeutics \/ Roche a annonc\u00e9 l\u2019arr\u00eat du dirloctocog\u00e8ne samoparvovec (SPK 8011, vecteur viral ad\u00e9no-associ\u00e9 avec g\u00e8ne FVIII humain supprim\u00e9 par le domaine B) chez les adultes pr\u00e9sentant une h\u00e9mophilie A s\u00e9v\u00e8re ou mod\u00e9r\u00e9ment s\u00e9v\u00e8re.<\/li>\n<\/ul>\n<p>L\u2019EHC souhaite exprimer sa gratitude au <a href=\"https:\/\/www.ehc.eu\/governance\/novel-treatment-review-ntr-committee\/\" target=\"_blank\" rel=\"noopener\"><strong>groupe de travail EHC NTR<\/strong><\/a> pour leur contribution au d\u00e9veloppement de cette question.<\/p>\n\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"bottom mt-12\" data-scroll data-fade-up>\n\t\t\t\t\t\t\t\t<a href=\"https:\/\/academy.ehc.eu\/wp-content\/uploads\/2025\/01\/NTR-January-2025.pdf\" target=\"_blank\" class=\"btn with-icon\">\n\t\t\t\t\t\t\t\t\t<span>Read the EHC NTR 2025 Issue One<\/span>\n\t\t\t\t\t\t\t\t<\/a>\n\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t<\/div>\n\t\t\t<\/div>\n\t\t<\/div>\n\t<\/section>\n\n<p><\/p>\n","protected":false},"excerpt":{"rendered":"<p>L\u2019EHC a publi\u00e9 le premier num\u00e9ro 2025 de son Novel Treatment Review (NTR), une revue p\u00e9riodique des nouveaux traitements dans les troubles h\u00e9morragiques rares.<\/p>\n","protected":false},"author":4,"featured_media":3498,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"_jetpack_memberships_contains_paid_content":false,"footnotes":""},"categories":[64],"tags":[146],"class_list":["post-6056","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-nouvelles","tag-ntr"],"acf":[],"jetpack_featured_media_url":"https:\/\/etngbd86n6b.exactdn.com\/wp-content\/uploads\/2025\/01\/NTR-Jan-2025-Blog-banner.jpg?strip=all&sharp=1","jetpack_sharing_enabled":true,"_links":{"self":[{"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/posts\/6056","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/users\/4"}],"replies":[{"embeddable":true,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/comments?post=6056"}],"version-history":[{"count":2,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/posts\/6056\/revisions"}],"predecessor-version":[{"id":6064,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/posts\/6056\/revisions\/6064"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/media\/3498"}],"wp:attachment":[{"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/media?parent=6056"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/categories?post=6056"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.ehc.eu\/fr\/wp-json\/wp\/v2\/tags?post=6056"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}