The publication of the first series focuses on gene therapy and haemophilia from both patient and expert points of view. The five-part series has been created to help patients and the general public understand and demystify some of the concepts related to gene therapy in haemophilia.
This series is the first major piece of patient-focused discussion and education about gene therapy and haemophilia.
What is gene therapy? with Prof. Flora Peyvandi
An overview in gene therapy for haemophilia A and B with Dr. Paul Giangrande
How does a clinical trial in gene therapy for haemophilia work? with Dr. Dan Hart
Safety and gene therapy with Prof. Michael Makris
Gene therapy: A patient’s perspective with Jack Grehan