On 9-11 September 2022, the European Haemophilia Consortium (EHC) will hold its Workshop on Health Economics with a focus on tenders and Procurement for rare bleeding disorders.
| What | The EHC Workshop on Health Economics focuses on Tenders and Procurement |
| When | 9-11 September 2022 |
| Where | Malmö, Sweden |
| For whom | Patient representatives, healthcare professionals, and government officials nominated by EHC members from Western and Central Europe |
| Registrations | Registrations will open from 21 June 2022 until 9 August 2022 |
| More information | Contact Laura Savini |
Programme
| 16.00-18.00 hrs | Registrations |
| 19.30-21.30 hrs | Welcome dinner |
| 09.00-10.35 hrs | Session 1: Getting up to speed with data and figures in haemophilia | |
| 09.00-09.05 | Welcome and introduction | |
| 09.05-09.35 | An update on treatment in haemophilia A | |
| 09.35-09.40 | Q&A | |
| 09.40-09.55 | From data to models: The terminology, the inputs and the pitfalls | |
| 09.55-10.00 | Q&A | |
| 10.00-10.30 | An update on treatment in haemophilia B | |
| 10.30-10.35 | Q&A and closing of the session | |
| 10.35-11.00 hrs | Panel discussions: Do we have enough data and information to make an informed decision? | |
| 11.00-11.30 hrs | Break | |
| 11.30-13.00 hrs | Session 2: Getting up to speed with data on VWD and other rare bleeding disorders and economic concepts | |
| 11.30-11.35 | Welcome and introduction | |
| 11.35-12.05 | An update on treatments in VWD and other RBD | |
| 12.05-12.10 | Q&A | |
| 12.10-12.30 | From data to models: The outputs and what they do not say | |
| 12.30-12.35 | Q&A | |
| 12.35-12.55 | Using economic analysis to advocate: The Canadian case study | |
| 12.55-13.00 | Q&A, poll, a summary of the session and next steps | |
| 13.00-14.15 hrs | Lunch | |
| 14.15-15.15 hrs | Session 3: How to develop and consider information for a country evaluation? | |
| 14.15-14.20 | Welcome and introduction | |
| 14.20-14.40 | What are the difficulties with the data? Perspectives from payers and regulators | |
| 14.40-15.00 | Paying for uncertainty – Thoughts for the future | |
| 15.00-15.10 | Q&A | |
| 15.10-15.15 | Closing of the session | |
| 15.15-15.30 hrs | Break | |
| 15.30-16.30 hrs | Group work: Hands-on with an economic model | |
| 15.30-15.45 | Presenting the exercise | |
| 15.45-16.15 | Group exercises | |
| 16.15-16.30 | Presenting the exercise results | |
| 16.30-17.00 hrs | Break | |
| 17.00-18.15 hrs | Session 3 – Continued | |
| 17.00-17.05 | Welcome | |
| 17.05-17.45 | Mock technical appraisal: Introduction to gene therapy | |
| 17.45-18.00 | Feedback | |
| 18.00-18.15 | Discussions and closing remarks for the day | |
| 19.45-21.45 hrs | Workshop Dinner | |
| 09.00-10.30 hrs | Session 4: Focus on procurement – Finding the best fit | |
| 09.00-09.05 | Welcome and introduction | |
| 09.05-09.25 | Using value frameworks: Comparing treatment options’ data | |
| 09.25-09.30 | Q&A | |
| 09.30-09.50 | Finding the suitable pricing model for procurement – From scoresheets to long-term agreements | |
| 09.50-09.55 | Q&A | |
| 09.55-10.15 | How do different procurement approaches affect cost-effectiveness? | |
| 10.15-10.20 | Q&A | |
| 10.20-10.30 | Session closing and take-aways | |
| 10.30-11.00 hrs | Break | |
| 11.00-11.50 hrs | Mock technical appraisal: The introduction of VWD concentrate | |
| 11.50-12.00 | Break | |
| 12.00-12.45 | Panel discussions: Creating innovative procurement for bleeding disorders | |
| 12.45-13.00 | Workshop conclusions and wrap up | |
| 13.00-14.30 | Lunch and departures | |
The EHC wishes to thank Pfizer, Sanofi and Sobi for their financial support of this event.
Jim is aged 66 and has Haemophilia A with a high titer inhibitor which he developed at age 14.
Maria Elisa Mancuso (MD, PhD) is a Haematologist and works as a Senior Haematology Consultant at the Center for Thrombosis and Haemorrhagic Diseases of IRCCS Humanitas Research Hospital in Rozzano, Milan, Italy. She is Adjunct Clinical Professor at Humanitas University. She obtained a post-degree in Clinical and Experimental Haematology and a PhD in Clinical Methodology. She is involved in clinical research and has published several original articles in peer-reviewed journals a The Lancet, Blood, Journal of Thrombosis and Haemostasis, Haematologica, Thrombosis and Haemostasis, British Journal of Haematology and Haemophilia. She is reviewer for several peer-reviewed journals and member of the Editorial Board of JTH. She is a member of several scientific societies (ISTH, WFH, ASH, EAHAD, SISET, AICE) and was a medical member of the Inhibitor Working Group of the European Hemophilia Consortium. She is co-chair of the ADVANCE Study Group. She has acted also as co-chair of the Scientific and Standardization Subcommittee of ISTH on FVIII, FIX and rare bleeding disorders. She has been involved as principal and co-investigator in several clinical trials, and she takes care of both children and adults with hemophilia and other congenital bleeding disorders with a specific scientific interest in novel therapies, prophylaxis, inhibitors, and chronic hepatitis C.
As a patient with factor II deficiency, the diagnostic and treatment of rare bleeding disorders is a matter dear to my heart. My motivation to participate in the work of the ERIN committee is to improve both diagnostic and treatment for patients with rare bleeding disorders across Europe.
Economist and financial expert by profession, executive coach and trainer by passion and haemophilia advocate by every drop of my blood through my son (who has severe haemophilia A with inhibitors). Bringing a good decade of practical experience from the corporate insurance world, laser focus, growth mindset and resilience from my own experience, offering you anything I can just do, in hope that together we can make life more fulfilled for those impacted by bleeding disorders.
Amy Owen-Wyard is a Registered Mental Health Nurse. With experience working with children, young people, their families and adults with severe and enduring mental health conditions. Amy was also involved in a service improvement to provide a holistic care approach for those in general hospitals to support both their mental and physical health, whilst sharing her expertise and knowledge in mental health with the wider multidisciplinary team.
